A Randomized, Double-Blind, Four-Arm Study Comparing Combination Nucleoside, Alternating Nucleoside, and Triple-Drug Therapy for the Treatment of Advanced HIV Disease (CD4 <= 50/mm3)

NCT ID: NCT00000781

Last Updated: 2021-11-04

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

1292 participants

Study Classification

INTERVENTIONAL

Study Completion Date

1996-09-30

Brief Summary

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To determine the relative clinical efficacy of zidovudine ( AZT ) plus didanosine (ddI), AZT plus zalcitabine ( ddC ), AZT alternating monthly with ddI, and AZT/ddI plus nevirapine in HIV-infected patients with advanced disease.

The rapid emergence of resistant HIV strains has been observed in patients receiving monotherapy with a nucleoside analog or non-nucleoside reverse transcriptase inhibitor. Use of combination therapy with two nucleoside drugs or convergent combination therapy with two nucleosides and a non-nucleoside RT inhibitor may minimize the evolution of these resistant HIV strains. Since toxicity is a major problem in patients with advanced disease who are receiving combination nucleoside therapy, alternating the two drugs may provide a way of retaining several benefits of combination therapy while minimizing the increased toxicity.

Detailed Description

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The rapid emergence of resistant HIV strains has been observed in patients receiving monotherapy with a nucleoside analog or non-nucleoside reverse transcriptase inhibitor. Use of combination therapy with two nucleoside drugs or convergent combination therapy with two nucleosides and a non-nucleoside RT inhibitor may minimize the evolution of these resistant HIV strains. Since toxicity is a major problem in patients with advanced disease who are receiving combination nucleoside therapy, alternating the two drugs may provide a way of retaining several benefits of combination therapy while minimizing the increased toxicity.

Patients are randomized to receive either AZT/ddC, AZT/ddI, AZT alternating monthly with ddI, or AZT/ddI/nevirapine. Patients are evaluated at week 0 and every 4 weeks thereafter for 2 years. Pharmacologic, virologic, and macroneurologic substudies will be conducted. Patients who are already enrolled on protocol ACTG 193 will be given the option of continuing on their originally assigned ACTG 193 therapy for an additional 6 months or undergoing re-randomization to one of the four treatment arms on ACTG 193A.

Conditions

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HIV Infections

Keywords

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Zalcitabine Didanosine Drug Therapy, Combination Acquired Immunodeficiency Syndrome Zidovudine Nevirapine

Study Design

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Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Interventions

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Nevirapine

Intervention Type DRUG

Zidovudine

Intervention Type DRUG

Zalcitabine

Intervention Type DRUG

Didanosine

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

Concurrent Medication:

Required:

* PCP prophylaxis.

Allowed:

* Erythropoietin maintenance.
* G-CSF and GM-CSF.
* Prophylaxis for Mycobacterium avium intracellulare.
* Antifungal prophylaxis or treatment with specific drugs.
* Maintenance therapy for opportunistic infection.
* Over-the-counter medications or alternative therapies such as vitamins and herbs.
* Antibiotics as clinically indicated.
* Steroids for \< 21 days for acute problems.
* Antipyretics, analgesics, allergy medication, antidepressants, sleep medications, oral contraceptives, or other appropriate medications.

Concurrent Treatment:

Allowed:

* Radiation therapy for cutaneous Kaposi's sarcoma.
* Acupuncture.

Patients must have:

* Documented HIV infection.
* CD4 count \<= 50 cells/mm3.
* Either no prior nucleoside therapy OR a history of prior nucleoside therapy in the absence of high-grade intolerance.
* Life expectancy of at least 6 months.
* Consent of parent or guardian if \< 18 years of age.
* Normal chest x-ray at baseline or within 6 months prior to study entry in the absence of new pulmonary or cardiac symptoms (per 12/28/94 amendment).

NOTE:

* Patients who withdrew from protocol ACTG 193 therapy prior to activation of ACTG 193A are not eligible.

Exclusion Criteria

Co-existing Condition:

Patients with the following symptoms or conditions are excluded:

* Abnormal baseline chest x-ray.
* New pulmonary or cardiac symptoms.
* Psychological or emotional problems sufficient to prevent compliance with study medication.

Concurrent Medication:

Excluded:

* Systemic chemotherapy for malignancy.
* Acute or induction therapy for opportunistic infection.
* Antiretroviral drugs other than study drugs.
* Biological response modifiers.
* Erythromycin, phenytoin, phenobarbital, warfarin, or coumadin.

Patients with the following prior conditions are excluded:

* History of recurrent grade 3 or greater toxicity to AZT, ddI, or ddC on two or more occasions.
* Evidence of active pulmonary disease within 6 months prior to study entry.
* History of grade 3 or worse peripheral neuropathy.
* History of acute or chronic pancreatitis.

Prior Medication:

Excluded:

* Prior nevirapine.

Excluded within 7 days prior to study entry:

* Acute therapy for opportunistic infection (maintenance therapy is permitted).
* Acute systemic therapy for a nonopportunistic infection or other medical condition.
* Antiretroviral drugs other than AZT, ddI, or ddC.
* Biological response modifiers.
* d4T therapy.
* Nucleosides other than those used in the study.
* Antibiotics containing clavulanate potassium.

Prior Treatment:

Excluded:

* More than 4 units of blood in a 30-day period.

Active alcohol or drug abuse.
Minimum Eligible Age

13 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Bristol-Myers Squibb

INDUSTRY

Sponsor Role collaborator

Glaxo Wellcome

INDUSTRY

Sponsor Role collaborator

National Institute of Allergy and Infectious Diseases (NIAID)

NIH

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Henry WK

Role: STUDY_CHAIR

Kahn JO

Role: STUDY_CHAIR

Balfour HH

Role: STUDY_CHAIR

Locations

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Univ of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Children's Hosp of Los Angeles

Los Angeles, California, United States

Site Status

Univ of Southern California / LA County USC Med Ctr

Los Angeles, California, United States

Site Status

Huntington Memorial Hosp / Children's Hosp of Los Angeles

Pasadena, California, United States

Site Status

Univ of California / San Diego Treatment Ctr

San Diego, California, United States

Site Status

San Francisco AIDS Clinic / San Francisco Gen Hosp

San Francisco, California, United States

Site Status

San Francisco Gen Hosp

San Francisco, California, United States

Site Status

Stanford at Kaiser / Kaiser Permanente Med Ctr

San Francisco, California, United States

Site Status

Santa Clara Valley Med Ctr / AIDS Community Rsch Consortium

San Jose, California, United States

Site Status

San Mateo AIDS Program / Stanford Univ

Stanford, California, United States

Site Status

Stanford Univ Med Ctr

Stanford, California, United States

Site Status

Olive View Med Ctr

Sylmar, California, United States

Site Status

Harbor UCLA Med Ctr

Torrance, California, United States

Site Status

Denver Dept of Health and Hosps

Denver, Colorado, United States

Site Status

Mountain States Reg Hemo Ctr / Univ of Colorado

Denver, Colorado, United States

Site Status

Rose Med Ctr

Denver, Colorado, United States

Site Status

Univ of Colorado Health Sciences Ctr

Denver, Colorado, United States

Site Status

Yale Univ / New Haven

New Haven, Connecticut, United States

Site Status

HIV Ctr - District of Columbia Gen Hosp

Washington D.C., District of Columbia, United States

Site Status

Whitman - Walker Clinic / Georgetown Univ Med Ctr

Washington D.C., District of Columbia, United States

Site Status

Georgetown Univ Med Ctr

Washington D.C., District of Columbia, United States

Site Status

George Washington Univ / Hershey Med Ctr

Washington D.C., District of Columbia, United States

Site Status

Howard Univ

Washington D.C., District of Columbia, United States

Site Status

Univ of Miami School of Medicine

Miami, Florida, United States

Site Status

Univ of South Florida

Tampa, Florida, United States

Site Status

Univ of Hawaii

Honolulu, Hawaii, United States

Site Status

Northwestern Univ Med School

Chicago, Illinois, United States

Site Status

Cook County Hosp

Chicago, Illinois, United States

Site Status

Rush Presbyterian - Saint Luke's Med Ctr

Chicago, Illinois, United States

Site Status

Louis A Weiss Memorial Hosp

Chicago, Illinois, United States

Site Status

Indiana Univ Hosp

Indianapolis, Indiana, United States

Site Status

Methodist Hosp of Indiana / Life Care Clinic

Indianapolis, Indiana, United States

Site Status

Univ of Louisville / East Tennesee Comprehensive Hem Ctr

Louisville, Kentucky, United States

Site Status

Harvard (Massachusetts Gen Hosp)

Boston, Massachusetts, United States

Site Status

Boston Med Ctr

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess - West Campus

Boston, Massachusetts, United States

Site Status

Worcester Memorial Hosp / Med Ctr of Cntrl MA-Memorial

Worcester, Massachusetts, United States

Site Status

Hennepin County Med Clinic

Minneapolis, Minnesota, United States

Site Status

Univ of Minnesota

Minneapolis, Minnesota, United States

Site Status

St Paul Ramsey Med Ctr

Saint Paul, Minnesota, United States

Site Status

St Louis Regional Hosp / St Louis Regional Med Ctr

St Louis, Missouri, United States

Site Status

Univ of Nebraska Med Ctr

Omaha, Nebraska, United States

Site Status

Dartmouth - Hitchcock Med Ctr / Med Ctr Cntrl Massachusetts

Lebanon, New Hampshire, United States

Site Status

Robert Wood Johnson Med School / Hershey Med Ctr

New Brunswick, New Jersey, United States

Site Status

Univ of Medicine & Dentistry of New Jersey / Univ Hosp

Newark, New Jersey, United States

Site Status

Adirondack Med Ctr at Saranac Lake

Albany, New York, United States

Site Status

Albany Med College / Division of HIV Medicine A158

Albany, New York, United States

Site Status

Mid - Hudson Care Ctr

Albany, New York, United States

Site Status

SUNY / Health Sciences Ctr at Brooklyn

Brooklyn, New York, United States

Site Status

SUNY / Erie County Med Ctr at Buffalo

Buffalo, New York, United States

Site Status

City Hosp Ctr at Elmhurst / Mount Sinai Hosp

Elmhurst, New York, United States

Site Status

North Shore Univ Hosp

Manhasset, New York, United States

Site Status

Beth Israel Med Ctr

New York, New York, United States

Site Status

Bellevue Hosp / New York Univ Med Ctr

New York, New York, United States

Site Status

Saint Clare's Hosp and Health Ctr

New York, New York, United States

Site Status

Cornell Univ Med Ctr

New York, New York, United States

Site Status

Mem Sloan - Kettering Cancer Ctr

New York, New York, United States

Site Status

Mount Sinai Med Ctr / Hemophilia Treatment Ctr

New York, New York, United States

Site Status

Mount Sinai Med Ctr

New York, New York, United States

Site Status

Columbia Presbyterian Med Ctr

New York, New York, United States

Site Status

Harlem Hosp Ctr

New York, New York, United States

Site Status

Univ of Rochester Medical Center

Rochester, New York, United States

Site Status

SUNY / State Univ of New York

Syracuse, New York, United States

Site Status

Bronx Municipal Hosp Ctr/Jacobi Med Ctr

The Bronx, New York, United States

Site Status

Comprehensive Health Care Ctr / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Montefiore Drug Treatment Ctr / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Montefiore Family Health Ctr / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Samaritan Village Inc / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Jack Weiler Hosp / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Montefiore Med Ctr / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Montefiore Med Ctr Adolescent AIDS Program

The Bronx, New York, United States

Site Status

North Central Bronx Hosp / Bronx Municipal Hosp

The Bronx, New York, United States

Site Status

Bronx Veterans Administration / Mount Sinai Hosp

The Bronx, New York, United States

Site Status

Univ of North Carolina

Chapel Hill, North Carolina, United States

Site Status

Moses H Cone Memorial Hosp

Greensboro, North Carolina, United States

Site Status

Univ of Cincinnati

Cincinnati, Ohio, United States

Site Status

Univ of Kentucky Lexington

Cincinnati, Ohio, United States

Site Status

Case Western Reserve Univ

Cleveland, Ohio, United States

Site Status

MetroHealth Med Ctr

Cleveland, Ohio, United States

Site Status

Columbus Children's Hosp

Columbus, Ohio, United States

Site Status

Med College of Ohio

Toledo, Ohio, United States

Site Status

Milton S Hershey Med Ctr

Hershey, Pennsylvania, United States

Site Status

Saint Michael's Med Ctr / Milton S Hershey Med Ctr

Hershey, Pennsylvania, United States

Site Status

Girard Med Ctr

Philadelphia, Pennsylvania, United States

Site Status

Univ of Pennsylvania at Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Thomas Jefferson Univ Hosp

Philadelphia, Pennsylvania, United States

Site Status

Med Univ of South Carolina / UNC

Charleston, South Carolina, United States

Site Status

Julio Arroyo

West Columbia, South Carolina, United States

Site Status

Univ of Tennessee / E Tennessee Comprehensive Hemophilia Ctr

Knoxville, Tennessee, United States

Site Status

Meharry Med College

Nashville, Tennessee, United States

Site Status

Univ of Texas Galveston

Galveston, Texas, United States

Site Status

Univ Texas Health Science Ctr / Univ Texas Med School

Houston, Texas, United States

Site Status

Univ of Washington

Seattle, Washington, United States

Site Status

Northern Wisconsin Hemophilia Ctr / Saint Vincent's Hosp

Green Bay, Wisconsin, United States

Site Status

Great Lakes Hemophilia Foundation

Wauwatosa, Wisconsin, United States

Site Status

Univ of Puerto Rico

San Juan, , Puerto Rico

Site Status

Countries

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United States Puerto Rico

References

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Henry K, Erice A, Tierney C, Balfour HH Jr, Fischl MA, Kmack A, Liou SH, Kenton A, Hirsch MS, Phair J, Martinez A, Kahn JO. A randomized, controlled, double-blind study comparing the survival benefit of four different reverse transcriptase inhibitor therapies (three-drug, two-drug, and alternating drug) for the treatment of advanced AIDS. AIDS Clinical Trial Group 193A Study Team. J Acquir Immune Defic Syndr Hum Retrovirol. 1998 Dec 1;19(4):339-49. doi: 10.1097/00042560-199812010-00004.

Reference Type BACKGROUND
PMID: 9833742 (View on PubMed)

Price RW, Yiannoutsos C, Zaborski L, Kmack A, Henry K, Tierney C, Clifford D. Neurological substudies of ACTG protocol 193A: quantitative neurological performance measures and treatment outcomes. Conf Retroviruses Opportunistic Infect. 1998 Feb 1-5;5th:176 (abstract no 516)

Reference Type BACKGROUND

Robinson P, Cotton D, Curry R, Henry K, Hall D, Myers M. Analysis of nevirapine (NVP) effect on clinical endpoints (CEs) of HIV progression or death in ACTG trial 193A. Conf Retroviruses Opportunistic Infect. 1998 Feb 1-5;5th:210 (abstract no 700)

Reference Type BACKGROUND

Henry K, Tierney C, Kahn J, Balfour H, Jiang Q, Kmack A, Fischl M. A randomized, double-blind, placebo-controlled study comparing combination nucleoside and triple therapy for the treatment of advanced HIV disease (CD4 less than or equal to 50/mm(3)). Conf Retroviruses Opportunistic Infect. 1997 Jan 22-26;4th:207 (abstract no LB6)

Reference Type BACKGROUND

Coplan P, Nikas A, Saah A, Nessly M, Doll L, Leavitt R, Benson J, Guess H. No association observed between indinavir therapy for HIV/AIDS and myocardial infarction in 4 clinical trials with 2,825 subjects. Conf Retroviruses Opportunistic Infect. 1999 Jan 31-Feb 4;6th:191 (abstract no 658)

Reference Type BACKGROUND

Erice A, Tierney C, Balfour HH Jr, Liou S, Kahn JO, Henry WK. Virologlc effect of therapy with reverse transcriptase inhibitors (RTIs) in patients with AIDS and less than 50 CD4+ T cells per mm(3): a substudy of ACTG 193a. Conf Retroviruses Opportunistic Infect. 1998 Feb 1-5;5th:204 (abstract no 662)

Reference Type BACKGROUND

Price RW, Yiannoutsos CT, Clifford DB, Zaborski L, Tselis A, Sidtis JJ, Cohen B, Hall CD, Erice A, Henry K. Neurological outcomes in late HIV infection: adverse impact of neurological impairment on survival and protective effect of antiviral therapy. AIDS Clinical Trial Group and Neurological AIDS Research Consortium study team. AIDS. 1999 Sep 10;13(13):1677-85. doi: 10.1097/00002030-199909100-00011.

Reference Type BACKGROUND
PMID: 10509569 (View on PubMed)

Other Identifiers

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11169

Identifier Type: REGISTRY

Identifier Source: secondary_id

ACTG 193A

Identifier Type: -

Identifier Source: org_study_id